https://ei-lca.com/wp-content/uploads/2026/03/immunity-versus-new-therapy-1.pdf

ei-lca.com/wp-content/u...
“Immunity versus new therapy”. A battle for greater influence inside the human eye, and when fiction could become reality. March 24, 2026.
@social.npo.one @fightblindness.bsky.social lindness.bsky.social @sarepta.com
#LCA10 #blindness

CNBC Cures 2026 Bringing together influential investors, policy makers and leaders in biotechnology to accelerate the future of medicine through breakthroughs in rare disease research.

www.cnbcevents.com/cures/
" It is a call to action: to reimagine healthcare, unlock bold new solutions, and accelerate a future where scientific breakthroughs for the rare disease community"
#LCA10 #blindness @cnbc.com @fightblindness.bsky.social
@retinauk.bsky.social @retinaint.bsky.social

SAVE THE DATE: 9-11 December 2025: High-Level Meeting on European Research and Innovation for Rare Diseases.
www.brains4brain.eu/save-the-dat...

@dubaieye.bsky.social #LCA10 #blindness #RNA #WRDD2026

@fnr.lu @middleeasteye-rss.bsky.social @iowalionseyebank.bsky.social @eye-tuebingen.bsky.social @newseye.bsky.social
Find more and read on (www.ei-lca.com)

29th Feb, 2026. #ZebraTales #CareAboutRare. @globalgenes.bsky.social
" The Shadow on the Eye" is a heart-stirring story that masterfully weaves two compelling threads: a tender exploration of multi-generational family bonds & an urgent, high-stakes scientific journey to cure LCA10
Read @ ei-lca.com

Leber Congenital Amaurosis Market Report 2025-2034: Industry Overview, Trends, And Forecast Analysis The Leber Congenital Amaurosis Market Report by The Business Research Company delivers a detailed market assessment covering size projections from 2025 to 2034 This report explores crucial market tren...

Leber Congenital Amaurosis Market Report 2025-2034: Industry Overview, Trends, And Forecast Analysis
04-25-2025
www.openpr.com/news/3987464...

Nordic Rare Disease Summit 2025 Act 2030: Pushing Boundaries for Rare - 16 & 17 September, Copenhagen

September 16 & 17, 2025; Copenhagen, Denmark
nordicrarediseasesummit.org#ABODesire
Nordic Rare Disease Summit 2025
Act 2030: Pushing Boundaries for Rare

#RareDisease #lca10

Opus Genetics Wins Rare Pediatric Disease designation from FDA Conexiant Vision: Delivering trusted clinical content, deep audience engagement, and educational resources for eye care professionals. Discover more through our magazines, newsletters, and events.

The FDA has granted its Rare Pediatric Disease designation to Opus Genetics’s OPGx-LCA5
www.ophthalmologymanagement.com/news/2024/op...

National Convention Virtual Experience | National Federation of the Blind Unable to attend convention in-person? Register for the virtual experience. Stream convention general sessions, access the app, and get a chance to win door prizes.

Register for the virtual experience. Stream convention general sessions, access the app, and get a chance to win door prizes.

July 8 through 13, 2025, plus pre-convention activities!
nfb.org/get-involved...
@fightblindness.bsky.social @riccobono.bsky.social #LCA10 #RareDisease #blindness

CANAIRI Co-Design Workshop - Canadian Rare Disease Network This workshop will co-design resources to support patients and families navigating the era of AI in medicine! The workshop is open to all and we welcome youth, adults, and families!

canadianrdn.ca/event/canair...
July 19th, Hybrid Workshop.
This workshop will co-design resources to support patients and families navigating the era of AI in medicine! The workshop is open to all and we welcome youth, adults, and families
@rnibradio.bsky.social #RareDisease #blindness

LA Community Connections - June Presentation Presentation by Dr. Jacque Duncan from UCSF

Wednesday, June 25th, 2025, 7:00 p.m. – 8:30 p.m. (PDT)
Presentation by Dr. Jacque Duncan from UCSF
www.fightingblindness.org/events/la-co...
@fightblindness.bsky.social @rnc.ac.uk #lca10 #RareDisease

@otdc-2026.bsky.social Oligonucleotide Therapeutics and Delivery Conference is all set to happen on March 23-24, 2026 as a hybrid event in Rome, Italy
oligo-nucleotide.com
#RareDisease #LCA10 #Blindness #oligonucleotide

Accelerate Ideas, Partnerships and Opportunities

Book your SLOT NOW

OTDC 2026
Oligonucleotide Therapeutics and Delivery Conference
March 23-24, 2026 | Rome, Italy

Website: oligo-nucleotide.com

RARE Advocacy Exchange Global Genes’ RARE Advocacy Exchange is a virtual event designed to empower, equip, and elevate individuals with the leadership skills to help make a change through a series of 8 sessions. We’re creat...

globalgenes.org/rare-advocac...
Global Genes’ RARE Advocacy Exchange is a virtual event designed to empower, equip, and elevate individuals with the leadership skills to help make a change through a series of 8 sessions.
@globalgenes.bsky.social #blindness #LCA10 #RareDisease

#LCA10 #blindness #raredisease #orphandrugs

www.retinaaustralia.com.au
Retina Australia funds and facilitates the top medical research into inherited retinal diseases (IRDs) through a competitive annual Research Grants Program.
#LCA10 #RareDisease #OrphanDrugs

Artificial intelligence (AI) is a computer program built to perform a specific task. It gets better at that task the more it does it. This ability to learn can solve problems in medical research.
eye2gene.com
#raredisease #lca10 #retina
@ucldiscovery.bsky.social

Study to Evaluate Sepofarsen in Subjects with Leber Congenital Amaurosis (LCA) Type 10 (HYPERION) (HYPERION)
clinical trial ID: NCT06891443
Sponsor- Laboratoires Thea. #blindness #LCA10 #CEP290
clinicaltrials.gov/study/NCT068...

Hope on the Horizon Blind people have a basic need to see. Novel therapeutic approaches are sorely needed for people suffering from CEP290-based disease. Scientists around the world work tirelessly to develop safe and…

Leber Congenital Amaurosis (LCA) is a rare inherited eye disorder that causes blindness in childhood.
ei-lca.com/hope-on-the-...

Gene therapy experiment treats rare childhood blindness Four toddlers born with a rare eye condition have seen

Groundbreaking gene therapy has restored vision in children born with leber congenital amaurosis (LCA), a severe genetic blindness.

www.bbc.co.uk/news/article...

1

Gene Therapy Shows Promise in Rare Eye Disease That Causes Early Blindness 'Mind-boggling' effects in small group with Leber congenital amaurosis 1, expert says

Gene therapy shows genuine promise in a rare eye disease that causes blindness. The condition is known as Leber congenital amaurosis-1 & there have been "mind-boggling" effects, an ophthalmologist says, referring to eyesight returning to these patients www.medpagetoday.com/ophthalmolog...

Doctors in London cure blindness in children with rare condition Four children can now see shapes, find toys, recognise their parents’ faces and some can read and write

Guardian: Doctors in London cure blindness in children with rare condition,
Leber congenital amaurosis

www.theguardian.com/society/2025...