To treat #cystinosis delayed-release #cysteamine (Procysbi®) improves adherence but is costly.
Interpretation: A newer version of the cystine depleting therapy has fewer daily doses but is expensive, limiting access for many.
Source: American Journal of Physiology-Renal Physiology, 🔗 in bio.
#Cysteamine must be taken lifelong, every 6 hours, to maintain cystine depletion in #cystinosis patients.
Interpretation: Patients take this medicine around the clock, every 6 hours, for life—missing doses risks organ damage.
Source: American Journal of Physiology-Renal Physiology, 🔗 in bio.
Early #cysteamine therapy delays ESRD but doesn’t cure #cystinosis or reverse #FanconiSyndrome.
Interpretation: Starting medication early buys time but doesn’t fix the kidneys or stop nutrient loss—it just slows decline.
Source: American Journal of Physiology-Renal Physiology, 🔗 in bio.
