#MDAConference: Ongoing trials are investigating the potential of restoring the #Frataxin protein in individuals with #FriedreichAtaxia (FA), despite the challenges this therapeutic approach presents. @mda.org
Read more: https://bit.ly/4ukONwp
Scientists are developing a one-time gene therapy that may target both nerve and heart complications in FA — something we’ve never had before.
Progress like this could change the game for our community.
Link in bio to read more. 🤍🌟 #FAResearch #Frataxin #RareDiseaseAwareness
