CME: Transforming Clinical Outcomes with Early Treatment of Lysosomal Disorders

Learn more at checkrare.com/learning/p-t...

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Reena Sharma, MD, Adult Metabolic Consultant at Salford Royal Hospital and University of Manchester, discusses plans for a phase 3 clinical trial evaluating FLT201 in patients with Gaucher disease.

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💡Rare Disease Spotlight: Gaucher Disease

Learn more about this rare disease with our latest article checkrare.com/a-global-col...

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Dawn Laney, genetic counselor at the Emory University School of Medicine, discusses a Fabry disease registry analysis examining growth in children being treated with agalsidase beta.

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Barbara Burton, MD, Professor of Pediatrics at Northwestern University Feinberg School of Medicine, discusses a recent study examining the effectiveness of idursulfase in young patients with MPS II.

checkrare.com/effectivenes...

#CheckRare #MPSII #RareLysosomal #RareMetabolic

💡Rare Disease Spotlight: Fabry Disease

Learn more about this rare disease at checkrare.com?s=Fabry+Dise...

#CheckRare #RareDisease #FabryDisease #RareLysosomal