Join us at #WORLDSymposium for interim results from the @ucsanfrancisco.bsky.social #PEARLTrial a first-in-human Phase 1 trial of In Utero #EnzymeReplacementTherapy for Lysosomal Disorders (PI Tippi MacKenzie). Presented by Billie Lianoglou: Thurs, Feb 6, 8:30 am #WORLDSymposia
pearltrial.ucsf.edu

Chiesi Global Rare Diseases to Showcase Groundbreaking Research at WORLDSymposium 2025 Chiesi Global Rare Diseases will present 11 important abstracts at the upcoming 21st Annual WORLDSymposium, focusing on Fabry disease and alpha-mannosidosis.

Chiesi Global Rare Diseases to Showcase Groundbreaking Research at WORLDSymposium 2025 #Italy #Rare_Diseases #Parma #Chiesi_Group #WORLDSymposium