Template-assisted sequence knock-in rescues skeletal and cardiac muscle function in a deletion model of Duchenne muscular dystrophy Cohn and colleagues demonstrate TASK, a CRISPR-mediated DNA integration strategy for full-length dystrophin restoration in a deletion mouse model of DMD. Precise integration of the missing exons into ...

Congrats to #ronald_cohn & colleagues for their new #MolTherapy paper: Template-assisted sequence knock-in rescues skeletal and cardiac muscle function in a deletion model of Duchenne muscular dystrophy. tinyurl.com/5x2sk6j2