๐#FDA Approval Update | #Avlayah: the first therapy targeting neurological symptoms of Hunter syndrome
๐ง Designed to cross the BBB, addressing a major unmet need in this #RareDisease
๐ ~91% reduction in #CSF heparan sulfate in trials
๐งชMCE provides tividenofusp alfa for research use
#HunterSyndrome
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