🧬 Intrathecal gene therapy for SMA may offer outcomes comparable to existing treatments.

An indirect comparison presented at #MDA2026 suggests Itvisma shows similar motor function improvements to nusinersen and risdiplam.

Visit NeurologyLive to read more‼️
#Neurology #SMA #GeneTherapy #RareDisease

✨ Hard to believe it’s been 2 weeks since launching the #RareAdvocacySpotlight with @mda.org!

Looking back at our #MDA2025 coverage — a great reminder of the innovation driving the rare disease community.

🎥 Explore the #MDA2026 agenda: https://bit.ly/4oBh8La

#RareDisease #MDAConference #MedSky