Our CEO Poul Sørensen shared our latest progress this morning at RNA Leaders in Vienna
#RNATherapeutics #Pseudoexon #Parkinsons #Huntingtons #RNAleaders
A deep intronic variant in PHKG2 caused #pseudoexon inclusion and GSD IX γ2 in two siblings, highlighting a pathway to detect and reverse non-coding splicing defects using RNA-seq and #antisensetherapy. bit.ly/4pMlNdS #GIMO #GlycogenStorageDisease #NonCodingVariants
Exciting news from Inverna ! 🎉
www.linkedin.com/posts/invern...
#RNATherapeutics #Pseudoexon #ASO #Innovation
Big news today! 🎉
#MJFF #RNAtherapeutics #Parkinsondisease #RNAsplicingmodulation #Pseudoexon #Innovation
Great pitching Inverna and our novel RNA splicing modulation platform at the BIO Europe Spring Startup Spotlight competition ! www.linkedin.com/posts/mads-a...
#RNAtherapeutics #Splicingmodulation #pseudoexon #innovation @invernatx.com