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#trofinetide
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A Phase 4 study shows the effectiveness and tolerability of #trofinetide for individuals with #Rettsyndrome
onlinelibrary.wiley.com/doi/10.1111/...

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#DMCNPodcast

Real-world benefits and tolerability of trofinetide for the treatment of Rett syndrome: The LOTUS study

#Rettsyndrome #Rett #trofinetide
www.youtube.com/watch?v=Dmun...

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