The April 2026 Cure GM1 Catalyst is out. Don't miss important highlights and progress in research, advocacy, and community efforts to advance treatments.
Engage, be informed, and share:
tinyurl.com/54navx8b
#curegm1 #raredisease #charity #hope #community
Enzyme replacement therapt (ERT) is one of the most direct and obvious ways to treat GM1. If you are in a position to donate, help or connect us with those who can, please reach out. Your help truly can make a difference.
LEARN MORE: curegm1.org/ert-project
#curegm1 #raredisease #charity #give
Happy National Puppy Day! Today, we’re remembering the special service dogs at our in-person annual conference last year.
Early registration is now open for our virtual conference: curegm1.org/conference
#curegm1 #raredisease #community #hope #charity
Join a powerful community of families, researchers, and advocates coming together to share knowledge, support, and hope. Early registration helps you plan ahead and ensures you don’t miss out on this meaningful event.
👉 Register now: curegm1.org/conference
#curegm1 #raredisease #community #hope
At just three years old, you’ve already shown what courage truly looks like. You are deeply loved, fiercely cherished, and surrounded by people who are cheering you on every single day.
Keep shining, Dominic. The world is brighter because of you!
#curegm1 #raredisease #hope #birthdays #charity
Your support can help accelerate the research needed to bring this therapy to forward to a clinical trial.
Please join us in supporting this critically important work.
MORE: curegm1.org/ert-project
#curegm1 #raredisease #hope #charity #give
When a child is diagnosed with conditions like cerebral palsy, developmental delay, or even just requires speech therapy, genetic testing could provide important answers. Those answers matter deeply.
LEARN: curegm1.org/gm1-gangliosidosis-symptoms
#curegm1 #raredisease #genetics #diagnosis
This St. Patrick’s Day, we’re sending a little extra luck to those living with rare diseases.
“Where there is hope, there is life.” — Anne Frank
May today bring strength, resilience, and moments of light to every rare warrior and their loved ones.
#curegm1 #raredisease #community #hope #charity
Learn more about the current status of AAV gene therapy as a potential treatment for GM1 gangliosidosis.
READ: curegm1.org/aav-gene-therapy-for-gm1
#curegm1 #raredisease #aav #genetherapy #research
From research updates and advocacy stories to practical guidance for families, our blogs are intended to empower and engage.
Together, informed voices strengthen the movement towards possible treatments.
🔗 Explore: curegm1.org/category/blo...
#curegm1 #raredisease #community #blog #hope
We invite you to become part of Friends of Cure GM1 Group, a community dedicated to raising awareness, supporting families, and accelerating research for a cure for GM1 gangliosidosis.
JOIN on FB: facebook.com/groups/1484265111658631
#curegm1 #raredisease #charity #nonprofit #hope
Every share, donation, and conversation raises awareness for GM1 families who urgently need help. Please join us in supporting this critically important work.
LEARN MORE: curegm1.org/ert-project
GIVE: curegm1.org/donate
#curegm1 #raredisease #charity #medicine #research
Because GM1 is a lysosomal storage disease, the missing enzyme causes harmful buildup inside cells throughout the body, not just in the central nervous system. This means organs, muscles, bones, and other tissues can also be affected.
LEARN: curegm1.org/about-gm1
#curegm1 #raredisease #medicine
GM1 gangliosidosis isn’t the same for every person affected. There are three main subtypes: Type 1, Type 2, Type 3. Each subtype has different ages of onset and progression.
🔗 curegm1.org/gm1-gangliosidosis-subtypes
Awareness -> understanding -> hope.
#curegm1 #raredisease #genetics #charity
Let’s continue working toward communities where everyone belong, where differences are respected, and inclusion is a priority. Together, we can build a world that recognizes ability, promotes understanding, and empowers every individual to thrive.
#curegm1 #awareness #disabled #raredisease
We are sending love to Marley on her ninth birthday on the 9th!
READ MORE: curegm1.org/marleys-story
#curegm1 #raredisease #hope #charity #awareness
On this International Women’s Day, we honor the caregivers, scientists, medical professionals and changemakers who show resilience and courage. Your voices matter, your work matters, and your impact is far-reaching.
#curegm1 #women #raredisease #community
A Carlsbad family is sharing the story of their 5-year-old son, Kiaan, who was diagnosed with GM1 gangliosidosis, an extremely rare genetic disorder that progressively damages nerve cells.
READ MORE: tinyurl.com/mrxx7hse
#curegm1 #raredisease #healthnews #medicalscience
“Loved beyond words, missed beyond measure.”
May sweet Ravi rest in heavenly peace.
#curegm1 #childloss #sweetangels #raredisease
Daxton was a joyful little boy whose life was tragically cut short by GM1 gangliosidosis, a rare and terminal genetic disease.
Read Daxton’s story and help bring hope to families fighting GM1:
curegm1.org/daxtons-story-2
#curegm1 #awareness #raredisease #genetics #charity
Thank you to our amazing community for the incredible submissions to our Rare Disease Day Photo Contest!
We were truly moved by the creativity, stories, and passion behind every photo shared.
#curegm1 #raredisease #community #advocacy #charity
Catch a quick update on advocacy, research progress, and ways our community advancing research for GM1.
SUBSCRIBE: curegm1.app.neoncrm.com/np/clients/curegm1/subscribe.jsp
NEWS: curegm1.org/march-2026-cure-gm1-catalyst
#curegm1 #raredisease #hope #advocacy #charity
The mission of Cure GM1 Foundation is to fund and accelerate research and drug development to advance possible treatments for GM1 gangliosidosis.
curegm1.org/take-action
#curegm1 #raredisease #takeaction #charity #donate
Thank you to everyone showed up for Rare Disease Day. Please continue standing with us.
Children continue to fight for life every single day, and the need for research and treatment remains critical.
LEARN: curegm1.org/about-gm1
#curegm1 #raredisease #advocacy #charity #hope
Today is Rare Disease Day!
Knowing the facts matters. Awareness leads to understanding. Understanding leads to action.
Take a moment today to learn about GM1 and other rare diseases. Start conversations. Share.
MORE: curegm1.org/about-gm1
#curegm1 #raredisease #genetics #advocacy #charity
Important Rare Disease Day coverage of GM1 and Kiaan's story! Watch and share.
WATCH: youtu.be/U-nnHHrFq-g?...
NEWS: tinyurl.com/ytcs8hyw
GIVE: tinyurl.com/mryd4hsr
P.S. The NIH runs the IV AAV9 trial
#curegm1 #raredisease #hope #donate #charity
GM1 is rare, but the need for awareness, research, and support is urgent. Every voice shared, every dollar donated, and every conversation started brings us one step closer to treatment. Join us.
LEARN: curegm1.org/about-gm1
GIVE: curegm1.org/donate
#curegm1 #raredisease #genetics #done #hope
Rare Disease Day is tomorrow. Please take a moment to read these stories.
Children and families living with rare diseases aren’t defined by diagnoses, they’re people first.
MORE: curegm1.org/stories
#curegm1 #hope #raredisease #advocacy #community #share
Knowing the facts matters. Awareness leads to understanding. Understanding leads to action.
Take a moment today to learn about GM1 and other rare diseases. Start conversations. Share.
MORE: curegm1.org/about-gm1
#curegm1 #raredisease #genetics #advocacy #charity
Celebrate hope for her birthday and Rare Disease Day. Treatments can change and save lives.
Give today. Share today. Help change the future.
WATCH: youtu.be/Thgwr8Grmy0?...
READ MORE: curegm1.org/kron4iris
GIVE: givebutter.com/SweetIris
#curegm1 #raredisease #donate #research #genetics
