Looking forward to contributing to the development of this evolving curriculum and to helping bring cutting-edge science closer to everyday clinical care 💊

#Rheumatology #MedicalEducation #EULAR #CellTherapy #GeneTherapy #Autoimmunity #Lupus

Watch today's Century Report podcast here:

https://www.youtube.com/watch?v=735bE_-NW4k

#AISafety #GeneTherapy #SolarEnergy

Every xAI cofounder is gone. Claude subscribers doubled during the Pentagon confrontation. Solar efficiency crossed the Shockley-Queisser limit. Gene therapy decoupled pain from addiction. #AISafety #GeneTherapy #SolarEnergy sharedsapience.com/century-report/the-centu...

Gene therapy: the only hope for Sydney sisters with ultra-rare genetic disease Sisters Mary and Neveah Taouk have PGAP1-CDG, one of the world's rarest genetic disorders. Their parents are funding gene therapy research.

Gene therapy: the only hope for Sydney sisters with ultra-rare genetic disease

#RareDisease #GeneTherapy #ChildHealth #MedicalResearch #AusNews

thedailyperspective.org/article/2026-03-29-gene-...

China's Hemophilia A Gene Therapy Partnership That Could Change Everything - AktieGo Belief BioMed and Grand Life Sciences partner to bring BBM-H803 gene therapy to 30,000 hemophilia A patients in China. Here's what it means for treatment access.

China is rewriting the rules for hemophilia treatment.
Exclusive partnership pushes cutting-edge gene therapy forward. Hope for thousands of patients just got real.
Don’t miss this biotech breakthrough →
aktiego.com/sectors/biot...
#GeneTherapy #Biotech #HemophiliaA #ChinaInnovation #Science

China's Hemophilia A Gene Therapy Partnership That Could Change Everything - AktieGo Belief BioMed and Grand Life Sciences partner to bring BBM-H803 gene therapy to 30,000 hemophilia A patients in China. Here's what it means for treatment access.

From lifelong injections to potential one-time cure?
This China hemophilia A gene therapy partnership is shaking up biotech. Could this be the breakthrough patients have been waiting for?
👉 aktiego.com/sectors/biot...
#GeneTherapy #BiotechRevolution #LifeSciences #HealthTech

Gene & Cell Therapy and Rare Disease Intelligence - LucidQuest Strategic insights for gene and cell therapy from R&D through commercialization. Primary KOL research, competitive analysis, and investment diligence in rare diseases.

🧬 Gene & Cell Therapy | #RareDiseases 🚀
#LucidQuest delivers sharp insights to help biotechs, investors & BD teams stay ahead in fast-moving markets.
📩 info@lqventures.com or http://dlvr.it/TRlGZt
#GeneTherapy #CellTherapy #Biotech #DueDiligence #InvestmentInsights

Pharmalittle: We're reading about Novo Nordisk boosting consumer focus, FDA approving a gene therapy, and more Novo Nordisk appointed Poul Weihrauch, CEO of the Mars candy company, as board observer as it tries to boost its consumer focus

Pharmalot.. Pharmalittle.. Good Morning: We’re reading about Novo Nordisk boosting consumer focus, FDA approving a gene therapy, and more news.. statnews.com/pharmalot/20... #pharma #FDA #genetherapy #obesity #depression #hepatitisC

Touchdown for Rocket as its first gene therapy gets US okay Rocket Pharma has won FDA approval for the first gene therapy for LAD-I, a devastating genetic disorder causing severe vulnerability to infections.

At its second attempt, #RocketPharma has won #FDA approval for its #genetherapy for severe leukocyte adhesion deficiency type I (LAD-I), a rare and life-threatening #immunedisorder that leaves patients vulnerable to life-threatening #infections.

Roatán-based longevity clinic adds Klotho to its non-permanent gene therapy lineup, widening its bet on high-end healthspan medicine.

Link as first comment.

#longevity #geroscience #genetherapy #healthspan

Immortal Dragons-backed Unlimited Bio registers world-first dual gene therapy trial to target age-related muscle loss and vascular decay.

Link as first comment.

#longevity #geroscience #genetherapy #muscle #vascular

What will you achieve in 4 weeks? 📋 Each team will develop:
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Apply by April 3. 🔗
tinyurl.com/genehpt
#GeneH #GeneTherapy #GeneTherapyAccelerator #HorizonEurope

Dr. Russell Lonser, Professor and Chair of The Ohio State University Department of Neurological Surgery, presented the 12th Annual Raymond Sawaya Lecture this morning to a full and attentive audience.

Dr. Russell Lonser presented the 12th Annual #BCMNeurosurgery Raymond Sawaya Lecture this morning to a full and attentive audience.

Many thanks to Dr. Lonser for sharing his insights on #GeneTherapy!

#Neurosurgery | #GrandRounds | #NeurosurgeryResidency | #MedEd

BioPharma (+ Google) Corporate Venture Capital Investment Trends: Who is leading in 2025? Get instant access to a concise analysis of 22 BioPharma (+ Google) CVCs and their portfolios. In minutes, you’ll see where strategic capital is flowing across Technology and Therapy Areas—and how 2025 trends compare to 2023. What’s inside: Clear mapping of CVC focus by Technology and Therapy Areas Trend shifts vs. 2023 to validate your thesis Actionable insights to spot momentum early How it works: Fill out the form to receive your report immediately. Questions or feedback? info@lqventures.com LucidQuest empowers BioPharma executives and Life Sciences investors with up-to-date analysis. Stay tuned for 2025 deep dives on Cell & Gene Therapy, Digital Health, Oncology & Hematology, and more.

What’s shaping CVC investments for 2025? Key trends: AI/ML, Gene Therapy, and a focus on Immune Disorders & Neurodegenerative Diseases. Curious for more? 📥 Download the full report for insights! http://dlvr.it/TRgYnN
#CVC #InvestingInInnovation #VentureCapital #GeneTherapy #AI

Can gene therapy transform sickle cell survival in Africa? Gene-editing breakthroughs are bringing curative therapies closer to reality. The challenge now is ensuring African health systems are ready to deliver them.

Science is proving a cure is possible. The real question is whether health systems are ready to deliver it where it’s needed most.

My latest for Nature Africa:

www.nature.com/articles/d44...

#sicklecell #genetherapy #africa

HSV Virus + Immunosuppressant Bortezomib Achieves Efficient Neuron Infection! HSV virus injection into L5 DRG neurons in mice, enhanced by bortezomib immunosuppressant, significantly increases neuronal infection and gene marker expression.

🔬 Enhancing HSV Virus Infection in Neurons with Bortezomib 🧠💉
📊 Key Findings:
▶️Bortezomib + HSV boosts virus efficiency in neuron infection.
▶️Enhanced EYFP labeling reveals over 50% of neurons in L5 DRG were successfully tagged.
🔗 www.ebraincase.com/support/lite...

#Neuroscience #GeneTherapy #HSV

4 weeks to market readiness. 📈 Our intensive program covers:
🔹W1: Innovation Pathways. 🔹W2: Regulatory (ATMPs). 🔹W3: Business Strategy. 🔹W4: Pitch.
Finish with a Demo Day to showcase your project!
Apply now! 🔗 forms.office.com/e/eRWZ2kdz3q
#GeneH #GeneTherapy #GeneTherapyAccelerator #HorizonEurope

🤝The #GeneTherapyAccelerator connects you to a "Quadruple Helix" network:
Academic, Industry, Clinical, and Policy experts from the #GeneH consortium. 🌐
Access the mentorship you need to succeed.
Apply by April 3! 🔗 forms.office.com/e/eRWZ2kdz3q
#GeneTherapy #HorizonEurope
@kemijski.bsky.social

Sensorion Reports Sustained Efficacy in Hearing Gene Therapy Sensorion on Mar 23, 2026 reported a 12-month mean PTA gain of 14.5 dB in n=18 patients with no treatment-related SAEs, per company release and Investing.com.

Sensorion Reports Sustained Efficacy in Hearing Gene Therapy: Sensorion on Mar 23, 2026 reported a 12-month mean PTA gain of 14.5 dB in n=18 patients with no treatment-related SAEs, per company release… 👈 Read full analysis #GeneTherapy #HearingLoss #Audiology #HealthcareInnovation #ClinicalTrials

🚀 Big buzz at #ASGCT25: #GeneEditing & #CRISPR headlines, 20% data-driven talk, 85% positive vibes on breakthrough therapies for #DMD & #rarediseases!🧬 Download our full #socialmedia report! http://dlvr.it/TRdbxW #GeneTherapy #SocialListening #LucidQuest
@ASGCTherapy @ESGCT

New Gene Therapy Trial Moves Forward Thanks to Chan Zuckerberg Initiative Backing from CZI’s Rare As One program led to a first in the push to treat FOXG1.

Backing from CZI’s Rare As One and CZI Ventures led to a first in the push to treat FOXG1.

Wendy Paris(@wendyparis.bsky.social) Reports: tinyurl.com/w33yj4rr

#RareDisease #GeneTherapy #MedicalResearch #BiotechInnovation #Philanthropy #ChanZuckerbergInitiative #HealthEquity #PatientAdvocacy

#Highlight in @medcomm.bsky.social #MedComm

#OTOF Gene Therapy: From Breakthroughs to Roadmaps doi.org/10.1002/mco2...

The highlighted article in #NatureMedicine : doi.org/10.1038/s415...

#ClinicalTrials #GeneTherapy

Cell Highlight丨Breaking Through AAV Delivery Bottlenecks! AAVLINK Technology Efficiently Delivers Large Genes to Aid in Genetic Disease Treatment AAVLINK enables efficient delivery of large genes for genetic diseases and CRISPR tools, overcoming challenges in gene splitting and neuron-specific expression.

🔬Literature Insight|AAVLINK: Efficient Large Gene Delivery for Genetic Disease Treatment
AAVLINK enables efficient delivery of large genes and CRISPR tools, overcoming AAV limitations for diseases like autism with optimized vectors.
👉 www.ebraincase.com/support/lite...
#GeneTherapy #AAVLINK #CRISPR

Gene from High Altitude Yak Protected and Repaired Myelin Sheath in Early MS Study A special gene that helps animals like the yak survive at high altitude could enable new treatments for multiple sclerosis after positive findings from a mouse model. The genetic mutation that enables yaks to live in environments with much less oxygen, and may hold the key to repairing nerve damage in conditions such as multiple […] The post Gene from High Altitude Yak Protected and Repaired Myelin Sheath in Early MS Study appeared first on Good News Network.

Gene from High Altitude Yak Protected and Repaired Myelin Sheath in Early MS Study: A special gene that helps animals like the yak survive at high altitude could enable new treatments for multiple sclerosis after… @goodnewsnetwork.org #MultipleSclerosis #MSResearch #GeneTherapy #Yaks #MyelinSheath

Can mRNA deliver what liver IMDs need?

In our latest Podcast, we discuss mRNA therapy for liver inherited metabolic diseases including protein replacement, liver targeting with LNPs, and the appeal of flexible repeat dosing.

open.spotify.com/episode/6umZ...

#mRNA #genetherapy #raredisease

x.com/aubreydegrey...
"Feb 6
Outstanding interview with George Church, one of the foremost superheroes of the longevity movement: "
www.youtube.com/watch?v=EvhO...
#biotech #genetherapy #vaccines #ambrosia 🧪🔬🧬

Gene & Cell Therapy and Rare Diseases' Research We conduct extensive research into the rapidly evolving gene and cell therapy and rare diseases arena to empower clients to win. Our strategic insights identify key players and developments, tailored to support BioPharma partners across R&D, clinical, regulatory, and commercial endeavors. The gene and cell therapy space has advanced rapidly, with new assets targeting therapeutic areas such as oncology, immunology, cardiovascular, CNS, and rare diseases. With multiple companies active and new approvals happening, it’s critical to get strategic insights, whether you are a BioPharma company or investor. Market and competitor insights on R&D, clinical development and commercial activities Extensive congress coverage, supporting brand owners with up-to-date intelligence Landscape analysis strengthened by expert interviews BD&L support Due diligence research New opportunity identification Access to experts’ opinion through a combination of in-house expertise and conduct of bespoke interviews We also invite you to join our LinkedIn Gene, Cell and RNA Therapy Strategy Network group – a hub for networking and information. Reach out to info@lqventures.com to learn more about our strategic consulting and research capabilities.

🧬 Gene & Cell Therapy | #RareDiseases 🚀
#LucidQuest delivers sharp insights to help biotechs, investors & BD teams stay ahead in fast-moving markets.
📩 info@lqventures.com or http://dlvr.it/TRZ8Sh
#GeneTherapy #CellTherapy #Biotech #DueDiligence #InvestmentInsights

Fixing gene chaos inside sick cells is the goal. Researchers need to sift through *millions* of chemicals to find ones that can precisely reset gene activity. 🧬 #genetherapy

Source: phys.org/news/2026-03-ai-chemical...

A CIRM-funded trial by @RocketPharma offers hope for LAD-1, a rare immune disease. All nine trial participants had their immune function restored by a #GeneTherapy that successfully treated the life-threatening disorder.

Read the story of the Langenhops: https://bit.ly/4uP7EQy

With the comprehensive information and assessment gathered using these guidelines, they aim to streamline the transition of CRISPR therapeutics from bench to bedside. (5/5)

#CRISPR #GeneTherapy #RareDisease #BiomedicalResearch