#MPSAwarenessDay #MPSVI #GeneTherapy #RareDiseases #LysosomalDisorders #TIGEM #FondazioneTelethon #MEUSIX #ClinicalTrials #TranslationalResearch #HopeForRare

Fetal therapy offers hope for unborn patients suffering from the rare genetic disease Hunter Syndrome Some parents-to-be have to face the terrifying news that their unborn child has been diagnosed with a life-threatening genetic disorder.

Today, May 15, we proudly observe #MPSAwarenessDay and stand in solidarity with the #MPS community. We thank our patients who participated in the prenatal ERT #PEARLTrial. Their courage and their contributions are humbling. Meet one of these inspiring families: bit.ly/3OgxCZD #MPSAwarenessDay2025