Trial Results Support Use of Patisiran in ATTR-PN Patisiran treatment showed a consistent positive effect across several endpoints in patients with a V122I or T60A variant-associated ATTR-PN.

#Patisiran treatment showed consistent positive effect across several endpoints, including #Polyneuropathy manifestations in patients with a #V122I or #T60A variant in the #TTR gene, in a multicenter phase 4 #ClinicalTrial

Read more: https://bit.ly/48CO8hm

#RareDisease #ATTRPN #MedSky

Sharing again as the #v122i #amyloidosis community is far too underrepresented. Please repost.