Mit #Donidalorsen ist ein weiteres Medikament zur Prophylaxe von Attacken des hereditären Angioödems #HAE verfügbar. Das Antisense-Oligonukleotid senkte in Studien die Häufigkeit der Attacken um 81 Prozent und kann ab einem Alter von zwölf Jahren eingesetzt werden.
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Long-term prophylaxis with #Donidalorsen administration every 4 weeks was associated with a significant reduction in creatine kinase levels in patients with #HereditaryAngioedema (HAE). Study in World Allergy Organization Journal.
Read more: https://bit.ly/4sgeQDm
#RareDisease #HAE
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Angioedema ereditario, ok Ue a prima terapia preventiva mirata all'Rna ... LEGGI TUTTO #Angioedema #Ereditarietà #Salute #Terapia #Donidalorsen
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Following FDA approval, #donidalorsen (Dawnzera) shows strong efficacy and safety in patients switching from other #HAE prophylactic therapies.
William Lumry, MD, discusses pivotal switch data and real-world impact: www.hcplive.com/view/switchi...
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