Missed our session with Dr. Thomas Coates on Sickle Cell Disease and Gene Therapy?

The full recording is now available on our YouTube channel!

➡️Watch the full session: youtu.be/TDNCgKR3p18?...

#GeneTherapy #SickleCellGeneTherapy #SickleCellDisease #Hematology #CellTherapy #RareDiseases

🧬The second question of the day focuses on how patient-reported outcomes reflect clinical benefit after Casgevy therapy.

#Casgevy #GeneTherapy #CRISPRGeneEditing #SickleCellGeneTherapy #SickleCellDisease #Hematology #CellTherapy #TranslationalMedicine #ClinicalTrials #RareDiseases #BloodDisorders

Additional results from the Exa-cel study.

Focus: CLIMB SCD-121 Trial

#Casgevy #GeneTherapy #CRISPRGeneEditing #SickleCellGeneTherapy #SickleCellDisease #Hematology #CellTherapy @ash.hematology.org @asgct.bsky.social @genesndiseases.bsky.social @bsochaem.bsky.social @ash.edu.hematology.org

Our session with Dr. Thomas Coates is in 2 weeks!

Don’t miss this opportunity to hear from a top expert in the field!

🔗Register now:
hemehub.org/live-events

#Casgevy #GeneTherapy #CRISPRGeneEditing #SickleCellGeneTherapy #SickleCellDisease #Hematology #CellTherapy #TranslationalMedicine

Further results from the Exa-cel study.

Focus: CLIMB SCD-121 Trial

#Casgevy #GeneTherapy #CRISPRGeneEditing #SickleCellGeneTherapy #SickleCellDisease #Hematology #CellTherapy #TranslationalMedicine #ClinicalTrials #RareDiseases #BloodDisorders #StemCellTherapy #HematopoieticStemCells

🩸 Today’s question addresses long-term safety considerations for patients treated with Lyfgenia, focusing on which risks require ongoing surveillance.

#Casgevy #GeneTherapy #CRISPRGeneEditing #SickleCellGeneTherapy #SickleCellDisease #Hematology #CellTherapy #TranslationalMedicine #ClinicalTrials

Additional facts about the Exa-cel (Exagamglogene Autotemcel, Casgevy) Study

Focus: CLIMB SCD-121 Trial

#Casgevy #GeneTherapy #CRISPRGeneEditing #SickleCellGeneTherapy #SickleCellDisease #Hematology #CellTherapy #TranslationalMedicine #ClinicalTrials #RareDiseases #BloodDisorders

Facts about the Exa-cel (Exagamglogene Autotemcel, Casgevy) Study

Focus: CLIMB SCD-121 Trial

#Casgevy #GeneTherapy #CRISPRGeneEditing #SickleCellGeneTherapy #SickleCellDisease #Hematology #CellTherapy #TranslationalMedicine #ClinicalTrials #RareDiseases #BloodDisorders #StemCellTherapy

NHS to offer 'groundbreaking' sickle cell gene therapy The gene therapy Casgevy, which will now be offered to some patients in England, could help people live disease-free, experts say.

#haematology #Sicklecelldisease #sicklecellgenetherapy #genetherapy #geneeditingtherapy #Casgevy #Exacel @vertexpharma.bsky.social #NHS #haemoglobin #clinicaltrials #functionalcure @AmandaPritchard #geneeditingtool #Crispr #editedstemcells #NHSEngland #clinicaltrials
www.bbc.co.uk/news/article...