American Society of Gene & Cell Therapy and Orphan Therapeutics… First-of-its-kind venture to facilitate and catalyze development of deprioritized cell and gene therapies, supported by AI-enabled platform

We’re proud to announce a new partnership with Orphan Therapeutics Accelerator to launch CGTxchange – a first-of-its-kind, jointly owned marketplace for deprioritized CGTs, accelerating development for ultra-rare diseases. #ASGCT #OTXL

Learn more: https://bit.ly/3LuypaS

Innovative Partnership to Propel Development of Rare Disease Gene Therapies The ASGCT and Orphan Therapeutics Accelerator unite to enhance the commercialization of gene therapies for rare diseases, utilizing AI advancements.

Innovative Partnership to Propel Development of Rare Disease Gene Therapies #United_States #gene_therapy #Milwaukee #ASGCT #Orphan_Therapeutics

On the cover: Chan, Wong, and colleagues depict how epigen improves diabetes via pancreas, liver, and adipose tissue. Image credit: Ka-Ying Chan and Zuoze Hao.

The November issue of #MolecularTherapy is out now! Dive into the latest in #immunotherapy, #GeneTherapy, commercially pre-viable CGTs for rare diseases, and #GeneEditing. Read it now: http://dlvr.it/TP7vtZ
#ASGCT

Molecular Therapy Presents: Advancing AAV Technology The use of AAV, the gold-standard viral vector for gene therapy, has successfully progressed from preclinical studies to multiple FDA-approved therapies.…

TODAY: #MolecularTherapy Presents has an exciting webinar, Advancing #AAV Technology, at 10-11 AM CDT. Don't miss out on this free event; register now: http://dlvr.it/TNqHBN
#ASGCT #genetherapy 🧬

Molecular Therapy Presents: Advancing AAV Technology The use of AAV, the gold-standard viral vector for gene therapy, has successfully progressed from preclinical studies to multiple FDA-approved therapies.…

#MolecularTherapy Presents has an exciting webinar, Advancing #AAV Technology, on October 22 at 10-11 AM CDT with Drs. Çağla Aksu Küz and Susumu Uchiyama. Don't miss out; register today: http://dlvr.it/TNhYj4
#ASGCT #genetherapy 🧬

Molecular Therapy Presents: Advancing AAV Technology The use of AAV, the gold-standard viral vector for gene therapy, has successfully progressed from preclinical studies to multiple FDA-approved therapies.…

#MolecularTherapy Presents has an exciting webinar, Advancing #AAV Technology, on October 22 at 10-11 AM CDT with Drs. Çağla Aksu Küz and Susumu Uchiyama. Don't miss out; register today: http://dlvr.it/TNSBsh
#ASGCT #genetherapy 🧬

Chao and colleagues show an image of glioblastoma (red) treated with CF17 oncolytic virus (green). Image credit: Jianfei Chao.

#MolecularTherapy Oncology's Sept 2025 issue covers new research on #Nanobodies, #OncolyticViruses, #BaseEditing, and #TherapeuticTargets in #Cancer. Check it out today: http://dlvr.it/TN8jsh
#ASGCT

Molecular Therapy Presents: Advancing AAV Technology October 22, 2025 | 10:00 AM CT

Join our free #MolecularTherapy Presents webinar to explore the latest in #AAV manufacturing and capsid design for #genetherapy. Register here today: http://dlvr.it/TN6NQT
#ASGCT

The cover image shows pumpkin spice DNA. Formulation is a key component in the success of nucleic acid delivery. Sallah et al. investigated how the addition of cucurbit[n]urils (CBs) to cationic polymers altered the profile of DNA delivery, reducing inflammation but increasing expression. Image credit: John Tregoning, Charlotte Tregoning, and Sophie Tregoning.

The new issue of #MolecularTherapy Nucleic Acids is out now. This issue features original articles on replicon #RNA vaccination, #circRNA therapeutics, mRNA-encoded BiTE cancer therapy, and more. Read it today: http://dlvr.it/TMzM2n
#MTNA #ASGCT

Molecular Therapy Presents: Advancements in Pediatric Cancer Therapy. Wednesday, August 6, 2025 at 1 PM CT.

Join us for this free webinar on August 6th hosted by #ASGCT and learn more about #PediatricCancerTherapy:
http://dlvr.it/TM2Ln3

Back From #ASGCT!!!
TIGEM was pleased to take part in the ASGCT Conference 2025, where we had the opportunity to present our latest research and engage with the gene and cell therapy community!

@asgct.bsky.social

🌍 Attending #ASGCT2025 in #NewOrleans?
Don’t miss this Scientific Symposium hosted by the Coalition of International Gene Therapy Societies:

📌 Clinical Trials Around the Globe
🗓️ [Today, May 16th]
🕗 8:00 AM – 9:45 AM
📍 Room 293–296

#GeneTherapy #ASGCT #AAV #Retina #LiverGeneTherapy #RareDisease

Day 1 at ASGCT: Missing scientists, a gene editing failure, and a gene editing first The mood at the annual meeting of the American Society of Cell and Gene Therapy isn’t amazing. The biotech market has been bad for years. But many researchers tried to project confidence.

Las decisiones políticas siguen afectando a la #ciencia y a los #científicos: según avisan en @statnews.com, en el congreso anual de la Sociedad Estadounidense de Terapia Genética y Celular #ASGCT falta gente: www.statnews.com/2025/05/14/a...

Azitra, Inc. Unveils Key Findings at ASGCT on New Cancer Treatment Approach Azitra, Inc. presents promising results on ATR04-484 targeting EGFR inhibitor-associated rash at ASGCT 2025, showcasing innovative cancer therapy.

Azitra, Inc. Unveils Key Findings at ASGCT on New Cancer Treatment Approach #United_States #New_Orleans #Azitra #ASGCT #ATR04-484

We’re at #ASGCT in New Orleans, LA! Visit us at poster #1171 — 'Simplifying Multigene Vector Design and Construction for Streamlined Development of Complex Therapeutics' — tonight from 5:30 to 7:00 PM in Poster Hall I2.

Good morning, #ASGCT New Orleans!

We look forward to a week of discussing new research with you at booth #1711. Stop by to connect with our experts over coffee.

Be sure to check out our poster presentations Today at 5:30 PM and Thursday: #AAV #mRNA #NGS #QualityControl #CellTherapy #GeneTherapy

We’re all set up and ready to go at #ASGCT.

Come meet our team at stand 714 to see how #Optimer, oligo-based antibody alternatives, can target gene therapy payloads to specific sites of action in the body or help build better assays for drug discovery and drug development.

This Thursday at the #ASGCT in New Orleans: Sadik Kassim (Danaher), Kiran Musunuru (Penn) and yours truly will chart a fundamentally new map to #CRISPR cures. See you at 830a (Room 291) and at 10a (Hall F).
Image: Mary Cassatt "The Map" (1890)

The #ASGCT2025 Exhibit Hall opens tomorrow at 5:30 pm! Explore 300+ exhibitors showcasing cutting-edge vector technologies, cell manufacturing platforms, and analytical solutions advancing cell and gene therapy development. Map your route via the #ASGCT events app! #CGTinnovation

Grit Biotechnology Showcases Cutting-Edge Advances at ASGCT 2025 Annual Meeting Grit Biotechnology highlights innovative research in immunotherapy at the ASGCT 2025 annual meeting, presenting updates on promising clinical programs.

Grit Biotechnology Showcases Cutting-Edge Advances at ASGCT 2025 Annual Meeting #China #Shanghai #GRIT_Biotechnology #ASGCT #Vitalgen_BioPharma

ASGCT Annual Meeting | American Society of Gene & Cell Therapy Home

‪@asgct.bsky.social‬ has posted that the
#ASGCT websites have been restored. Thank you for your patience. There’s still time to register for the 28th Annual Meeting – either in-person or virtually! Advanced Registration pricing is open through May 12. Visit annualmeeting.asgct.org
for details.

#ASGCT websites have been restored. Thank you for your patience. There’s still time to register for the 28th Annual Meeting – either in-person or virtually! Advanced Registration pricing is open through May 12. Visit annualmeeting.asgct.org for details.

#ASGCT websites have been restored. Thank you for your patience. There’s still time to register for the 28th Annual Meeting – either in-person or virtually! Advanced Registration pricing is open through May 12. Visit annualmeeting.asgct.org
for details.

Always great to see the first person you meet on the way to a conference, especially the #ASGCT
Today I got to catch up with Guangping Gao from UMass Chan Medical School and chat about viral vectors and the exciting clinical progress to be presented at #ASGCT2025.
#AAV #CRISPR

#ASGCT is experiencing an unplanned website service disruption. We apologize for any inconvenience and are working to restore asgct.org as quickly as possible. For immediate support, please email info@asgct.org.

#ASGCT is experiencing an unplanned website service disruption. We apologize for any inconvenience and are working to restore asgct.org as quickly as possible. For immediate support, please email info@asgct.org.

PacBio is gearing up for #ASGCT2025 in New Orleans!

We’re excited to be part of the leading event for gene and cell therapy experts. Discover how HiFi sequencing is unlocking new possibilities in research and accelerating breakthroughs across the field.

#PacBio #ASGCT

Join our team next week at #ASGCT to see how Optimer can help with:
🎯Targeted delivery for your gene therapy
🧪Custom reagents to build better assays
🔍 Identify new biomarkers of disease

Don’t miss our poster
📊 ‘Targeted Delivery of siRNA to Activated Hepatic Stellate Cells Using Aptamers’

Apertura Gene Therapy Unveils Breakthrough AAV Capsid Progress at ASGCT 2025 Apertura Gene Therapy highlights its innovative AAV capsid, TfR1 CapX, at ASGCT, showcasing advancements in targeting neurological disorders through gene therapy.

Apertura Gene Therapy Unveils Breakthrough AAV Capsid Progress at ASGCT 2025 #United_States #New_Orleans #ASGCT #Apertura_Gene #TfR1_CapX

Specific Biologics Inc. Unveils Dualase Genome Editing at ASGCT Meeting Specific Biologics Inc. is set to present its innovative Dualase® genome editing platform aimed at treating repeat expansion disorders during the ASGCT meeting in New Orleans.

Specific Biologics Inc. Unveils Dualase Genome Editing at ASGCT Meeting #USA #New_Orleans #ASGCT #Specific_Biologics #Dualase